Category: Perspectives on Current Science

  • New Miniature CRISPR-Cas Systems Engineered to Function in Human Cells

    New Miniature CRISPR-Cas Systems Engineered to Function in Human Cells

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  • President’s Pick of Presentations from the Annual OTS Meeting

    President’s Pick of Presentations from the Annual OTS Meeting

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  • 2021 Annual Meeting Highlights

    2021 Annual Meeting Highlights

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  • Non-Profits Create Next-Generation Medicines that Treat Ultra-Rare Diseases

    Non-Profits Create Next-Generation Medicines that Treat Ultra-Rare Diseases

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  • Oligonucleotides Safely Cross the Blood-Brain Barrier to Knock Down Gene Expression

    Oligonucleotides Safely Cross the Blood-Brain Barrier to Knock Down Gene Expression

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  • OTS President’s Paper Pick – August 2021

    OTS President’s Paper Pick – August 2021

    By: Annemieke Aartsma-Rus, Ph.D. The paper information: CRISPR-Cas9 In Vivo Gene Editing for Transthyretin Amyloidosis Julian D Gillmore, Ed Gane, Jorg Taube, Justin Kao, Marianna Fontana, Michael L Maitland, Jessica Seitzer, Daniel O’Connell, Kathryn R Walsh, Kristy Wood, Jonathan Phillips, Yuanxin Xu, Adam Amaral, Adam P Boyd, Jeffrey E Cehelsky, Mark D McKee, Andrew Schiermeier, […]

  • Lipid Nanoparticles: Nanomedicine’s Triumph

    Lipid Nanoparticles: Nanomedicine’s Triumph

    [fusion_builder_container type=”flex” hundred_percent=”no” equal_height_columns=”no” hide_on_mobile=”small-visibility,medium-visibility,large-visibility” background_position=”center center” background_repeat=”no-repeat” fade=”no” background_parallax=”none” parallax_speed=”0.3″ video_aspect_ratio=”16:9″ video_loop=”yes” video_mute=”yes” border_style=”solid”][fusion_builder_row][fusion_builder_column type=”1_1″ layout=”1_1″ background_position=”left top” background_color=”” border_color=”” border_style=”solid” border_position=”all” spacing=”yes” background_image=”” background_repeat=”no-repeat” padding_top=”” padding_right=”” padding_bottom=”” padding_left=”” margin_top=”0px” margin_bottom=”0px” class=”” id=”” animation_type=”” animation_speed=”0.3″ animation_direction=”left” hide_on_mobile=”small-visibility,medium-visibility,large-visibility” center_content=”no” last=”true” min_height=”” hover_type=”none” link=”” border_sizes_top=”” border_sizes_bottom=”” border_sizes_left=”” border_sizes_right=”” first=”true”][fusion_text] Oligonucleotide therapeutics have been making headlines this […]

  • A Momentous CRISPR Milestone was Achieved with Remarkable Results

    A Momentous CRISPR Milestone was Achieved with Remarkable Results

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  • Oligonucleotide Therapeutics – Restoring Sight to the Blind

    Oligonucleotide Therapeutics – Restoring Sight to the Blind

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  • Can Oligonucleotides Target RNA Splicing to Treat Disease?

    Can Oligonucleotides Target RNA Splicing to Treat Disease?

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